ミグルスタット
- (グルコシルセラミド合成酵素阻害薬;I型ゴーシェ病治療
- a rarely used miscellaneous agent.
indications This drug is used to treat adults with mild to moderate type 1 Gaucher disease. contraindications Pregnancy and known hypersensitivity to this drug prohibit its use. Mosby's Medical Dictionary, 8th edition.
<click2in>http://en.wikipedia.org/wiki/Miglustat</click2in> <click2in>http://www1.actelion.com/en/scientists/development-pipeline/phase-4/miglustat-zavesca.page</click2in>